Overview:
Currently, there is no cure for SMA, although this may change with expanding treatment options. A rapidly changing treatment landscape is altering the clinical management of patients with SMA. Three therapies are currently FDA-approved and have dramatically impacted this condition. However, many health needs remain unmet in this patient population. As evidence of therapeutic effects continues to emerge, it is important for clinicians to be aware of evolving patient needs and strategies that can facilitate earlier diagnosis and more effective disease management. Furthermore, incorporating principles of diversity, equity, and inclusion (DEI) into SMA management is crucial to addressing disparities in healthcare outcomes among minority groups. By focusing on these areas, healthcare systems can better support the diverse needs of all SMA patients, fostering a more inclusive approach to care. Thus, this activity will feature expert discussing the assessment of bulbar function, use of novel therapies, and best practices for SMA management with a focus on minority patients.
Learning Objectives:
Upon completion of this activity, participants will be able to:
- Apply assessment techniques to accurately evaluate bulbar function in pediatric patients with spinal muscular atrophy (SMA)
- Analyze the latest safety and efficacy data of new disease-modifying therapies for SMA in pediatric patients
- Formulate strategies to overcome challenges in managing patients of minority groups with SMA
Emma Ciafaloni, MD
Professor of Neurology and Pediatrics
Department of Neurology-Neuromuscular Division
University of Rochester
Rochester, NY
Julie Parsons, MD
Professor of Pediatrics and Neurology
University of Colorado School of Medicine
Aurora, CO
Physicians’ Education Resource®, LLC is accredited by the Accreditation Council for Continuing Medical Education (ACCME) to provide continuing medical education for physicians.
Physicians’ Education Resource®, LLC designates this live activity for a maximum of 1.0 AMA PRA Category 1 Credits™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.
Physicians’ Education Resource®, LLC is approved by the California Board of Registered Nursing, Provider #16669, for 1.0 Contact Hours.